Design of an Observational Study to Assess Real-World Outcomes of Patients with Duchenne Muscular Dystrophy in the US Treated with Givinostat

Aravindhan Veerapandiyan, Erika L. Finanger, Emma Ciafaloni, Tina Duong, Crystal Proud, Carolina Tesi Rocha, Mary Jane Salinas, Sara Cazzaniga, Katiana Gruppioni, Thomas O. Crawford

Givinostat Effect on Respiratory Function in Duchenne Muscular Dystrophy Before and After Ambulation Loss: Results From EPIDYS, LTSE, and PRO-DMD-01 Studies

Eugenio Mercuri, Craig M. McDonald, Chamindra G. Laverty, Erika L. Finanger, James E. Signorovitch, Andrea Parodi, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Yann Péréon

Long-Term Safety of Givinostat in Patients With Duchenne Muscular Dystrophy: Results From an Open-Label Extension Study

John F. Brandsema, Gyula Acsadi, Nicoletta Coceani, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Erika L. Finanger