Vastus Lateralis Fat Fraction is Associated with Functional Efficacy Endpoints in Patients with Duchenne Muscular Dystrophy Treated with Givinostat in EPIDYS
Michela Guglieri, Craig M. McDonald, Francesco Bellanti, Sara Cazzaniga, Paolo Bettica, Ulrike Schara-Schmidt, Eugenio Mercuri, Nuria Muelas, Krista Vandenborne
Efficacy of Givinostat by Age (6–7 and >7 years): A Post Hoc Analysis of EPIDYS
Dragana Vucinic, Chamindra G. Laverty, Federica Alessi, Nicoletta Coceani, Paolo Bettica, Yoram Nevo
Disease Progression Modeling in Duchenne Muscular Dystrophy: Delayed Decay in 4-Stair Climb With Givinostat Compared With Standard of Care
Chamindra G. Laverty, Eugenio Mercuri, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Anna Largajolli, Francesco Bellanti, Yann Péréon, Craig M. McDonald, Erika L. Finanger
Modeling Disease Progression in Duchenne Muscular Dystrophy: Reduced Decline in Forced Vital Capacity With Givinostat Compared With Standard of Care
Erika L. Finanger, Chamindra G. Laverty, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Anna Largajolli, Francesco Bellanti, Yann Péréon, Craig M. McDonald, Eugenio Mercuri
Efficacy of Givinostat in the Off-Target Population of EPIDYS: A Subgroup Analysis
Chamindra G. Laverty, Han C. Phan, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Richard Finkel
Characterizing Gastrointestinal Adverse Events of Interest From a Phase 3 Study of Givinostat in Patients With Duchenne Muscular Dystrophy
Liesbeth De Waele, John F. Brandsema, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Erika L. Finanger
Thorough QT Study on the Effect of Therapeutic and Supratherapeutic Dosing of Givinostat in Healthy Volunteers
Tracey Willis, Eugenio Mercuri, Barry Byrne, Erik H Niks, Ulrike Schara-Schmidt, Thierry Le Tourneau, Odile Boespflug-Tanguy, Michela Guglieri, Nuria Muelas, David Gómez Andrés, Han C. Phan, Sergio César Díaz, John Bourke, Sara Cazzaniga
Cardiac Safety Data for Givinostat in Ambulant Patients with Duchenne Muscular Dystrophy: Results from EPIDYS Study
Tracey Willis, Eugenio Mercuri, Barry Byrne, Erik H Niks, Ulrike Schara-Schmidt, Thierry Le Tourneau, Odile Boespflug-Tanguy, Michela Guglieri, Nuria Muelas, David Gómez Andrés, Han C. Phan, Sergio César Díaz, John Bourke, Sara Cazzaniga
Characterizing Thrombocytopenia in Patients With Duchenne Muscular Dystrophy Treated With Givinostat: Results From the Phase 3 EPIDYS Trial
Laura McAdam, John Brandsema, Erika L. Finanger, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Erik H. Niks
Patient-Reported Outcomes From a Phase 3 Study of Givinostat in Patients With Duchenne Muscular Dystrophy
Liesbeth De Waele, Laura McAdam, Federica Alessi, Nuria Muelas, Katiana Gruppioni, Sara Cazzaniga, Paolo Bettica