Givinostat Effect on Respiratory Function in Duchenne Muscular Dystrophy Before and After Ambulation Loss: Results from EPIDYS, OLE, and PRO-DMD-01
Craig M. McDonald, Chamindra G. Laverty, Erika L. Finanger, James Signorovitch, Andrea Parodi, Federica Alessi , Sara Cazzaniga, Paolo Bettica, Yann Péréon, Eugenio Mercuri
Design of an Observational Study to Assess Real-World Outcomes of Patients with Duchenne Muscular Dystrophy in the US Treated with Givinostat
Erika L. Finanger, Emma Ciafaloni, Tina Duong, Crystal Proud, Carolina Tesi Rocha, Aravindhan Veerapandiyan, Mary Jane Salinas, Sara Cazzaniga, Katiana Gruppioni, Tom Crawford
Long-Term Safety of Givinostat in Patients with Duchenne Muscular Dystrophy: Results from an Open-Label Extension Study
John Brandsema, Gyula Acsadi, Nicoletta Coceani, Federica Alessi , Sara Cazzaniga, Paolo Bettica, Erika L. Finanger
Givinostat Efficacy in Duchenne Muscular Dystrophy: Natural History Comparison Applying Propensity Score Matching
David Gomez Andres, Valeria Sansone, Han C. Phan, Tracey Willis, Michela Guglieri, Mariacristina Scoto, Krista Vandenborne, Sara Cazzaniga, Nicoletta Coceani, Paolo Bettica, Craig M. McDonald
Efficacy of Givinostat in the Off-Target Population of EPIDYS: A Subgroup Analysis
Richard Finkel, Han C. Phan, Federica Alessi , Sara Cazzaniga, Paolo Bettica, Chamindra G. Laverty
Modeling Disease Progression in Duchenne Muscular Dystrophy: Reduced Decline in Forced Vital Capacity with Givinostat Compared with Standard of Care
Erika L. Finanger, Chamindra G. Laverty, Federica Alessi , Sara Cazzaniga, Paolo Bettica, Anna Largajolli, Francesco Bellanti, Yann Péréon, Craig M. McDonald, Eugenio Mercuri
Disease Progression Modeling in Duchenne Muscular Dystrophy: Delayed Decay in 4-Stair Climb with Givinostat Compared with Standard of Care
Chamindra G. Laverty, Eugenio Mercuri, Federica Alessi , Sara Cazzaniga, Paolo Bettica, Anna Largajolli, Francesco Bellanti , Yann Péréon, Craig M. McDonald, Erika L. Finanger