Givinostat Reduces the Decline of Contractile Cross-sectional Area and Decreases Fat Infiltration in Patients with Duchenne Muscular Dystrophy
Krista Vandenborne, Rebecca Wilcocks, Paolo Bettica, Sara Cassaniga, Federica Alessi, Eugenio Mercuri
Open-label Extension Analysis Shows Potential Delay in Age at Loss of Ambulation in Patients with Duchenne Muscular Dystrophy Treated with Givinostat
David Gomez Andres, Valeria Sansone, Andrea Parodi, Odile Boespflug-Tanguy, Natali Goedeker, Paolo Bettica, Tracey Willis, Eugenio Mercuri
Long-term Safety of Givinostat in Patients with Duchenne Muscular Dystrophy: Interim Results from an Open-label Extension Study
John F Brandsema, Gyula Acsadi, Federica Alessi, Paolo Bettica, Odile Boespflug-Tanguy, Michela Guglieri, Erika L, Finanger
Givinostat Weight-Based Flexible Dosing: Rationale and Efficacy at the Different Doses
Aravindhan Veerapandiyan, Federica Alessi, Sara Cazzaiga, Paolo Bettica, Eugenio Mercuri
Givinostat Reprograms TGFβ-Induced Fibrotic Networks in DMD Stromal Cells
Monica Forino, Andrea Ghiroldi, Christian Steinkuhler, Gianluca Fossati
Cardiac Safety Data for Givinostat in Ambulant Patients with Duchenne Muscular Dystrophy: Results from the EPIDYS Study
Eugenio Mercuri, Barry J Byrne, Erik H Niks, Ulrike Schara-Schmidt, Tracey Willis, Theirry Le Tourneau, Odile Boespflug, Tanguy, Michela Guglieri, Nuria Muelas, David Gomez Andres, Han C Phan, Sergio Cesar Diaz, John Bourke, Sara Cazzaniga
Characterizing Gastrointestinal Adverse Events of Interest From a Phase 3 Study of Givinostat in Patients With Duchenne Muscular Dystrophy
Liesbeth De Waele, John F Brandsema, Federica Alessi, Sara Zazzaniga, Paolo Bettica, Erika L Finanger
Characterizing Thrombocytopenia in Patients With Duchenne Muscular Dystrophy Treated With Givinostat: Results From the Phase 3 EPIDYS Trial
Laura McAdam, John F Brandsema, Erika L Finanger, Federica Alessi, Sara Zaxxaniga, Paolo Bettica, Erik H Niks
Characterizing Platelet Count Reductions Below 75 x 10^9/L in Patients with Duchenne Muscular Dystrophy Treated with Givinostat from the Phase 3 EPIDYS Trial and LTSE Study
Michela Guglieri, Maria Cristina Scoto, Mary Jane Salinas, Andrea Parodi, Paolo Bettica, Erika L. Finanger
A Simplified Givinostat Dosing Regimen Minimizes Exposure Differences and Dose Reductions in Higher-Weight Patients
Eugenio Mercury, Francesco Bellanti, Sara Cassaniga, Paolo Bettica, Craig McDonald