Disease Progression Modeling in Duchenne Muscular Dystrophy: Delayed Decay in 4-Stair Climb With Givinostat Compared With Standard of Care
Chamindra G. Laverty, Eugenio Mercuri, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Anna Largajolli, Francesco Bellanti, Yann Péréon, Craig M. McDonald, Erika L. Finanger