Design of an Observational Study to Assess Real-World Outcomes of Patients with Duchenne Muscular Dystrophy in the US Treated with Givinostat
Erika L. Finanger, Emma Ciafaloni, Tina Duong, Crystal Proud, Carolina Tesi Rocha, Aravindhan Veerapandiyan, Mary Jane Salinas, Sara Cazzaniga, Katiana Gruppioni, Thomas O. Crawford