Vastus Lateralis Fat Fraction is Associated with Functional Efficacy Endpoints in Patients with Duchenne Muscular Dystrophy Treated with Givinostat in EPIDYS

Craig M. McDonald, Francesco Bellanti, Sara Cazzaniga, Paolo Bettica, Ulrike Schara-Schmidt, Eugenio Mercuri, Michela Guglieri, Nuria Muelas Gómez, Krista Vandenborne

Characterizing Thrombocytopenia in Patients With Duchenne Muscular Dystrophy Treated With Givinostat: Results From the Phase 3 EPIDYS Trial

John F. Brandsema, Erika L. Finanger, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Laura McAdam, Erik H. Niks

Givinostat Effect on Respiratory Function in Duchenne Muscular Dystrophy Before and After Ambulation Loss: Results From EPIDYS, LTSE, and PRO-DMD-01 Studies

Craig M. McDonald, Chamindra G. Laverty, Erika L. Finanger, James E. Signorovitch, Andrea Parodi, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Yann Péréon, Eugenio Mercuri

Givinostat Weight-Based Flexible Dosing: Rationale and Efficacy at the Different Doses

Aravindhan Veerapandiyan, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Eugenio Mercuri