Givinostat Effect on Respiratory Function in Duchenne Muscular Dystrophy Before and After Ambulation Loss: Results From EPIDYS, LTSE, and PRO-DMD-01
Craig M. McDonald, Chamindra G. Laverty, Erika L. Finanger, James E. Signorovitch, Andrea Parodi, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Yann Péréon, Eugenio Mercuri
Long-Term Safety of Givinostat in Patients With Duchenne Muscular Dystrophy: Results From an Open-Label Extension Study
John F. Brandsema, Gyula Acsadi, Nicoletta Coceani, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Erika L. Finanger
Givinostat Efficacy in Duchenne Muscular Dystrophy: Natural History Comparison Applying Propensity Score Matching
David Gomez Andres, Valeria A. Sansone, Han C. Phan, Tracey Willis, Michela Guglieri, Mariacristina Scoto,Krista Vandenborne, Sara Cazzaniga, Nicoletta Coceani, Paulo Bettica, Craig M. McDonald
Thorough QT Study on the Effect of Therapeutic and Supratherapeutic Dosing of Givinostat in Healthy Volunteers
Eugenio Mercuri, Barry Byrne, Erik H. Niks, Ulrike Schara-Schmidt, Tracey Willis, Thierry Le Tourneau, Odile Boespflug-Tanguy, Michela Guglieri, Nuria Muelas, David Gomez Andres, Han C. Phan, Sergio Cesar Diaz, John Bourke, Sara Cazzaniga
Efficacy of Givinostat in the Off-Target Population of EPIDYS: A Subgroup Analysis
Richard Finkel, Han C. Phan, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Chamindra G. Laverty
Modeling Disease Progression in Duchenne Muscular Dystrophy: Reduced Decline in Forced Vital Capacity With Givinostat Compared With Standard of Care
Erika L. Finanger, Chamindra G. Laverty, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Anna Largajolli, Francesco Bellanti, Yann Péréon, Craig M. McDonald, Eugenio Mercuri
Patient-Reported Outcomes From a Phase 3 Study of Givinostat in Patients With Duchenne Muscular Dystrophy
Laura McAdam, Federica Alessi, Nuria Muelas, Liesbeth De Waele, Katiana Gruppioni, Sara Cazzaniga, Paolo Bettica, Craig M. Zaidman
Cardiac Safety Data for Givinostat in Ambulant Patients with Duchenne Muscular Dystrophy: Results from EPIDYS Study
Eugenio Mercuri, Barry Byrne, Erik H. Niks, Ulrike Schara-Schmidt, Tracey Willis, Thierry Le Tourneau, Odile Boespflug-Tanguy, Michela Guglieri, Nuria Muelas, David Gomez Andres, Han C. Phan, Sergio Cesar Diaz, John Bourke, Sara Cazzaniga
Disease Progression Modeling in Duchenne Muscular Dystrophy: Delayed Decay in 4-Stair Climb With Givinostat Compared With Standard of Care
Chamindra G. Laverty, Eugenio Mercuri, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Anna Largajolli, Francesco Bellanti, Yann Péréon, Craig M. McDonald, Erika L. Finanger