Efficacy of Givinostat by Age (6–7 and >7 years): A Post Hoc Analysis of EPIDYS
Chamindra G. Laverty, Federica Alessi, Nicoletta Coceani, Paolo Bettica, Dragana Vucinic
Vastus Lateralis Fat Fraction is Associated with Functional Efficacy Endpoints in Patients with Duchenne Muscular Dystrophy Treated with Givinostat in EPIDYS
Craig M. McDonald, Francesco Bellanti, Sara Cazzaniga, Paolo Bettica, Ulrike Schara-Schmidt, Eugenio Mercuri, Michela Guglieri