Disease Progression Modeling in Duchenne Muscular Dystrophy: Delayed Decay in 4-Stair Climb With Givinostat Compared With Standard of Care
Chamindra G. Laverty, Eugenio Mercuri, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Anna Largajolli, Francesco Bellanti, Yann Péréon, Craig M. McDonald, Erika L. Finanger
Characterizing Gastrointestinal Adverse Events of Interest From a Phase 3 Study of Givinostat in Patients With Duchenne Muscular Dystrophy
Erika L. Finanger, Liesbeth De Waele, Federica Alessi, Sara Cazzaniga, Paolo Bettica, John F. Brandsema
Characterizing Thrombocytopenia in Patients With Duchenne Muscular Dystrophy Treated With Givinostat: Results From the Phase 3 EPIDYS Trial
John Brandsema, Erika L. Finanger, Federica Alessi, Sara Cazzaniga, Paolo Bettica, Laura McAdam, Erik H. Niks